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Live Company Data
NMS
Updated
just now
· Data: FMP
Current Price
$56.07
+63.76%
+$21.83 today
Day: $54.98 – $57.10
52-Week Range
Current price is at 94% of 52-week range
⚠️ Financial data is for informational purposes only. Not investment advice. Prices may be delayed.
Indication
Spinal muscular atrophy (SMA), add-on to SMN-targeted therapy
Key Notes
BLA resubmitted in 2026 with FDA action expected in late September 2026 (PDUFA target near September 30, 2026). Selective myostatin inhibitor intended to improve motor function on top of nusinersen or risdiplam, based on the Phase 3 SAPPHIRE trial. First potential muscle-directed therapy in SMA. Source: Scholar Rock IR (BLA resubmission, 2026).
⚠️ Not Investment Advice: This information is provided for educational purposes only.
PDUFA dates are FDA target action dates, not guaranteed approval dates. The FDA may extend the review period,
issue Complete Response Letters, or take unexpected actions. Probability of approval scores are based on
historical base rates and do not account for drug-specific factors. Always consult a financial advisor
before making investment decisions.
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